{"id":13468,"date":"2025-12-16T16:00:00","date_gmt":"2025-12-16T16:00:00","guid":{"rendered":"https:\/\/icter.local\/seminar\/from-mechanisms-to-therapies-preventing-blindness-2\/"},"modified":"2025-12-16T16:00:00","modified_gmt":"2025-12-16T16:00:00","slug":"from-mechanisms-to-therapies-preventing-blindness-2","status":"publish","type":"seminar","link":"https:\/\/icter.jcd.pl\/pl\/seminar\/from-mechanisms-to-therapies-preventing-blindness-2\/","title":{"rendered":"From Mechanisms to Therapies Preventing Blindness"},"content":{"rendered":"<p>Opracowanie skutecznych metod leczenia dziedzicznych i nabytych chor\u00f3b prowadz\u0105cych do utraty wzroku nadal pozostaje du\u017cym wyzwaniem. Jedn\u0105 z g\u0142\u00f3wnych przeszk\u00f3d jest niepe\u0142ne zrozumienie biologii oka oraz brak narz\u0119dzi umo\u017cliwiaj\u0105cych zar\u00f3wno dok\u0142adne poznanie mechanizm\u00f3w choroby, jak i precyzyjne oddzia\u0142ywanie terapeutyczne.<\/p>\n<p>Podczas seminarium dr Aleksander Tworak przedstawi trzy kierunki swoich bada\u0144, \u0142\u0105cz\u0105ce technologie multiomiczne, nowoczesne modele do\u015bwiadczalne oraz terapi\u0119 genow\u0105. Om\u00f3wi funkcj\u0119 bia\u0142ka MFRP, kt\u00f3rego mutacje prowadz\u0105 do ma\u0142oocza i zwyrodnienia siatk\u00f3wki, a tak\u017ce badania nad zale\u017cn\u0105 od \u015bwiat\u0142a regeneracj\u0105 barwnika wzrokowego i mo\u017cliwo\u015bciami wzmacniania tego procesu u pacjent\u00f3w. Zaprezentuje r\u00f3wnie\u017c prace nad uniwersaln\u0105 strategi\u0105 edycji gen\u00f3w dla jednogenowych chor\u00f3b siatk\u00f3wki, kt\u00f3ra mog\u0142aby by\u0107 stosowana niezale\u017cnie od rodzaju mutacji wywo\u0142uj\u0105cej chorob\u0119.<\/p>\n<h3>O prelegencie<\/h3>\n<p>Dr Aleksander Tworak jest adiunktem badawczym w Brunson Center for Translational Vision Research na Wydziale Okulistyki i Nauk o Widzeniu Uniwersytetu Kalifornijskiego w Irvine. Stopie\u0144 doktora z biochemii uzyska\u0142 w 2014 roku w Instytucie Chemii Bioorganicznej Polskiej Akademii Nauk w Poznaniu. Nast\u0119pnie odby\u0142 sta\u017c podoktorski w zespole prof. Marka Figlerowicza, po czym kontynuowa\u0142 badania na Case Western Reserve University oraz w laboratorium prof. Krzysztofa Palczewskiego w Kalifornii. Kieruje projektami badawczymi finansowanymi przez Velux Stiftung oraz Knights Templar Eye Foundation.<\/p>\n<p>Jego badania koncentruj\u0105 si\u0119 na fagocytozie zewn\u0119trznych segment\u00f3w fotoreceptor\u00f3w i procesach ich recyklingu w kom\u00f3rkach nab\u0142onka barwnikowego siatk\u00f3wki (RPE), a tak\u017ce na szlaku regeneracji barwnika wzrokowego z udzia\u0142em receptora RGR. Celem jego pracy jest lepsze poznanie mechanizm\u00f3w utrzymuj\u0105cych prawid\u0142owe funkcjonowanie siatk\u00f3wki oraz opracowanie nowych terapii zapobiegaj\u0105cych utracie wzroku.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Opracowanie skutecznych metod leczenia dziedzicznych i nabytych chor\u00f3b prowadz\u0105cych do utraty wzroku nadal pozostaje du\u017cym wyzwaniem. Jedn\u0105 z g\u0142\u00f3wnych przeszk\u00f3d jest niepe\u0142ne zrozumienie biologii oka oraz brak narz\u0119dzi umo\u017cliwiaj\u0105cych zar\u00f3wno dok\u0142adne poznanie mechanizm\u00f3w choroby, jak i precyzyjne oddzia\u0142ywanie terapeutyczne. Podczas seminarium dr Aleksander Tworak przedstawi trzy kierunki swoich bada\u0144, \u0142\u0105cz\u0105ce technologie multiomiczne, nowoczesne modele do\u015bwiadczalne [&hellip;]<\/p>\n","protected":false},"author":0,"featured_media":0,"comment_status":"","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"tags":[],"seminar-category":[],"coauthors":[],"class_list":["post-13468","seminar","type-seminar","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.9 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>From Mechanisms to Therapies Preventing Blindness - ICTER<\/title>\n<meta name=\"robots\" content=\"noindex, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<meta property=\"og:locale\" content=\"pl_PL\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"From Mechanisms to Therapies Preventing Blindness - ICTER\" \/>\n<meta property=\"og:description\" content=\"Opracowanie skutecznych metod leczenia dziedzicznych i nabytych chor\u00f3b prowadz\u0105cych do utraty wzroku nadal pozostaje du\u017cym wyzwaniem. 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